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Nicklaus Children’s Hospital has several outpatient and urgent care centers throughout South Florida, including on-demand, virtual care.
Walk-in urgent care with no appointment needed.
Serving as your child's primary doctor's office.
Pediatric specialty consultations available closer to home.
A full range of comprehensive services all under one roof.
Connect with providers from the comfort of your own home.
With over 800 pediatric clinicians on staff, we’re dedicated to helping you connect with the right specialist for your needs.
We have expertise in treating children and educating families on hundreds of different conditions.
We use cutting-edge, specialized treatments and procedures to ensure the best care for your child.
Also known as: DMD.
Muscular dystrophy is a genetic condition characterized by progressive muscle weakness, difficulties with movement and other symptoms. Duchenne muscular dystrophy is known for getting worse much more.
A genetic defect causes the body not to produce as much dystophin as it should. Dystrophin is a protein that helps strengthen muscles. However, it’s unclear why this defect occurs. It does not appear to run in families.
Progressive muscle weakness is the primary symptoms of Duchenne muscular dystrophy. This included problems with movement, falls and trouble getting up from sitting or lying down. Fatigue, learning problems and intellectual disability are other problems related to Duchenne muscular dystrophy.
Certain drugs such as steroids can slow the loss of muscle strength. Exercises and physical therapy can help those with Duchenne muscular dystrophy live the best life possible.
Reviewed by: Trevor J Resnick, MD
This page was last updated on: May 01, 2020 04:29 PM
Gene therapy offers the opportunity to treat a wide range of chronic and severe inherited diseases that previously had few to no treatment options.