Neuroscience Institute Clinical Trials

Randomized Study in Children and Adolescents With Migraine: Acute Treatment

Conditions: Pediatric Migraine.
Principal Investigator: Wilson Heredia Nunez.
Study ID: NEU23013 (C4951002-BHV3000-311) | View Study Details

Humanitarian Device Exemption (Dystonia IRB)

Conditions: Dystonia.
Principal Investigator: Toba Niazi.
Study ID: NEU99202 (H020007) | View Study Details

Focal Cerebral Arteriopathy Steroid Trial (FOCAS)

Conditions: Pediatric Stroke, Arteriopathy, Arterial Ischemic Stroke.
Principal Investigator: Anuj Jayakar.
Study ID: NEU23170 (FOCAS) | View Study Details

A Double-blind Study Evaluating the Efficacy, Safety, and Tolerability of Zorevunersen in Patients With Dravet Syndrome

Conditions: Dravet Syndrome.
Principal Investigator: Matt Lallas.
Study ID: NEU24048 (STK-001-DS-301) | View Study Details

Blood Brain Barrier (BBB) Disruption Using Exablate Focused Ultrasound With Doxorubicin for Treatment of Pediatric Diffuse Intrinsic Pontine Gliomas (DIPG)

Conditions: Brain Tumor.
Principal Investigator: Toba Niazi.
Study ID: NEU23134 (BT016) | View Study Details

A Study to Evaluate the Efficacy, Safety, and Tolerability of Brivaracetam as Monotherapy in Patients 2 to 25 Years of Age With Childhood Absence Epilepsy or Juvenile Absence Epilepsy (EXPAND)

Conditions: Childhood Absence Epilepsy, Juvenile Absence Epilepsy.
Principal Investigator: Anuj Jayakar.
Study ID: NEU23003 (N01269) | View Study Details

A Study to Investigate Behavioral and Other Co-Occurring Outcomes With Epidiolex as Add-On Therapy in Participants Aged 1 to 65 Years of Age With Tuberous Sclerosis Complex (EpiCom)

Conditions: Tuberous Sclerosis Complex Associated Neuropsychiatric Disease.
Principal Investigator: Paula Schleifer.
Study ID: NEU23103 (JZP926-402) | View Study Details

Phase 3 Efficacy and Safety Study of GTX-102 in Pediatric Subjects with AS (Aspire)

Conditions: Angelman Syndrome.
Principal Investigator: Paula Schleifer.
Study ID: NEU24001 (GTX-102-CL301) | View Study Details

Efficacy and Safety of Erenumab in Pediatric Participants With Episodic Migraine (OASIS(EM))

Conditions: Migraine.
Principal Investigator: Wilson Heredia Nunez.
Study ID: NEU23101 (20150125) | View Study Details

Study to Assess the Efficacy, Safety, and Tolerability of Valbenazine for the Treatment of Dyskinesia Due to Cerebral Palsy

Conditions: Dyskinesia, Cerebral Palsy.
Principal Investigator: Migvis Monduy.
Study ID: NEU99201 (NBI-98854-DCP3018) | View Study Details

A Study to Test the Long-term Safety and Tolerability of Brivaracetam in Study Participants With Childhood Absence Epilepsy or Juvenile Absence Epilepsy

Conditions: Childhood Absence Epilepsy' Juvenile Absence Epilepsy.
Principal Investigator: Anuj Jayakar.
Study ID: NEU24007 (EP0224) | View Study Details