Neuroscience Institute Clinical Trials

REVEAL: A Phase 3 Study of ION582 in Angelman Syndrome

Conditions: Angelman Syndrome.
Principal Investigator: Paula Schleifer.
Study ID: NEU24071 (ION582-CS2) | View Study Details

Focal Cerebral Arteriopathy Steroid Trial (FOCAS)

Conditions: Pediatric Stroke, Arteriopathy, Arterial Ischemic Stroke.
Principal Investigator: Anuj Jayakar.
Study ID: NEU23170 (FOCAS) | View Study Details

A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome (ENDEAVOR)

Conditions: Dravet Syndrome.
Principal Investigator: Matt Lallas.
Study ID: NEU24063(ETX-DS-002) | View Study Details

A Phase 3, Placebo-Controlled Study to Investigate LP352 in Children and Adults With Dravet Syndrome (DS)

Conditions: Dravet Syndrome.
Principal Investigator: Matt Lallas.
Study ID: NEU24088 (LP352-302) | View Study Details

A Study to Test the Long-term Safety and Tolerability of Brivaracetam in Study Participants With Childhood Absence Epilepsy or Juvenile Absence Epilepsy

Conditions: Childhood Absence Epilepsy' Juvenile Absence Epilepsy.
Principal Investigator: Anuj Jayakar.
Study ID: NEU24007 (EP0224) | View Study Details

Honeycomb: Evaluation of Radiprodil in Children with GRIN-related Disorder

Conditions: GRIN-related Disorders.
Principal Investigator: Matt Lallas.
Study ID: NEU24078 (20242004) | View Study Details

A Feasibility Safety Study of Benign Centrally-Located Intracranial Tumors in Pediatric and Young Adult Subjects

Conditions: Benign Centrally-Located Intracranial Tumors.
Principal Investigator: John Ragheb.
Study ID: NEU99205 (BT005) | View Study Details

A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome

Conditions: Rett Syndrome.
Principal Investigator: Paula Schleifer.
Study ID: NEU24062 (NGN RTT-200) | View Study Details