Austin's Success Story


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Ka'lee is Running, Walking and Thriving After Gene Therapy for Muscular Dystrophy

junio 19, 2026 – Ka'lee was diagnosed with Duchenne Muscular Dystrophy (DMD) at just two years old. One of four siblings, he is the only one in his family with this condition. His mother, Carmen, did not expect the diagnosis, and at first, didn't fully understand what it would mean for her son's future. Since his first treatment in 2024 he has achieved milestones that once felt out of reach.

Pequeña pero poderosa: Bebé de 1.2 lb sale de la UCI neonatal después de tres meses

marzo 04, 2026

Pocos días después del nacimiento de la bebé Pierson, cuando pesaba solo 1.2 lb, se colocó un pequeño catéter en su vena para entregar un dispositivo diminuto que trató su defecto cardíaco congénito, todo mientras permanecía en su incubadora.


Leading Pediatric Epilepsy Care for 40 Years

febrero 26, 2025 – For 40 years, Nicklaus Children's Hospital has been a leader in pediatric epilepsy. Learn more about the comprehensive care we offer for the most complex chronic cases.

Gene Therapy Offers New Hope for Children with Duchenne MD

enero 23, 2025 – At Nicklaus Children's Hospital, gene therapy offers a promising treatment that dramatically improves life for children with Duchenne muscular dystrophy. Recognizing the potential wielded by a new gene therapy, Nicklaus Children’s became one of the first in the nation to offer ELEVIDYS-dystrophin soon after the FDA's 2023 approval.